Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

A researcher can introduce the gene encoding the receptor protein to a small group of neurons using a viral vector. Then, ...

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. When 13-month-old Adam’s stem cell ...

GJB2 gene therapy enters human testing for the first time as Skylark Bio doses the first child in the SONIX Phase 1/2 trial, ...

Red blood cells serve as the foundation for nanocarriers that show promise in a new study as effective and efficient vehicles ...

Austin, United States, Aug. 13, 2026 (GLOBE NEWSWIRE)-- According to SNS Insider, the Adeno-Associated Virus (AAV) CDMO Market was valued at USD 0.61 billion in 2025 and is projected to reach USD 3.90 ...

A six-year-old Chinese girl died following a botched gene-therapy trial after her spine was infused with trillions of viruses in a bid to cure a non-life-threatening condition. The pathogens were ...